ALS-024

Amyotrophic Lateral Sclerosis (ALS)

Rome 60 years old male Italy Total Cost: 534

Patient Condition

The patient developed bulbar symptoms (dysarthria, dysphagia) at the age of 58, and was diagnosed with ALS (bulbar onset) at the age of 59. At the time of diagnosis, ALSFRS-R was 30, FVC was 68%, and swallowing function was impaired. Progress is rapid (monthly decrease of 1.3 points). Enrolled into the neural stem cell (NSC) phase I/II trial.

Treatment Timeline

PhaseDetailsDate
NSC treatment
Follow-up treatment and nutritional management
long-term follow-up

Treatment Outcome

beforeALSFRS-R 30, monthly drop 1.3, FVC 68%, bulbar onset
afterALSFRS-R 25 points, 2-year decrease of 5 points (84% delay), FVC 58%(BiPAP)
highlightNSC treatment in patients with bulbar onset ALS delays progression by 84% and significantly improves prognosis