FFI-012

Fatal familial insomnia (FFI)

Asia 47 years old male Japan Total Cost: 280

Patient Condition

The patient developed severe insomnia at the age of 45, which gradually developed into complete insomnia, accompanied by autonomic nervous dysfunction (tachycardia, hyperhidrosis, body temperature fluctuations). At the age of 47, fatal familial insomnia was diagnosed (FFI, PRNP D178N mutation, Met129 homozygous). At the time of diagnosis, complete insomnia lasted for 3 months, with an MMSE of 26 points, severe autonomic symptoms (blood pressure difference in supine and upright position> 40mmHg), and a significant decrease in heart rate variability. The expected survival period is 12 months.

Treatment Timeline

PhaseDetailsDate
Symptom control and sleep induction
Immunomodulation and symptomatic treatment
Long-term maintenance and palliative care

Treatment Outcome

beforeComplete insomnia 3 months, MMSE 26 points, severe autonomic nervous dysfunction, expected survival 12 months, PRNP D178N/Met129 homozygous mutation
afterSurvival period was extended to 28 months (still under follow-up), MMSE was 18 points, drug-induced sleep could be maintained for 4-6 hours a day, nutritional status was good, and no serious complications occurred
highlightDrug-induced sleep +IVIG immunomodulation extends the survival of patients with FFI by 130%, breaking expectations of rapid disease progression and providing new ideas for the treatment of prion diseases