China

Pediatric Hospital Affiliated to Fudan University, China

Shanghai

About

The Pediatric Hospital Affiliated to Fudan University is an important part of the National Children's Medical Center and is in a leading position in the country in the diagnosis and treatment of rare neurological diseases, genetic metabolic diseases and rare immunodeficiency diseases in children. The hospital has a special rare disease center and genetic diagnosis platform. It has accumulated rich experience in neonatal screening, genetic diagnosis and comprehensive treatment of spinal muscular atrophy (SMA), Duchenne muscular dystrophy and multiple genetic metabolic diseases. It is an important participant in the clinical research of new drugs for childhood rare diseases such as SMA.

Specialties

  • Rare neurological diseases in children
  • Spinal muscular atrophy (SMA)
  • genetic metabolic disease
  • primary immunodeficiency

Achievements

  • Core member units of the National Children's Medical Center
  • Participated in multiple clinical trials of new drugs for rare diseases in children such as SMA
  • Establish a rapid genetic diagnosis and prenatal diagnosis system for rare diseases in children