NEJM

Prime Editing for p47(phox)-Deficient Chronic Granulomatous Disease.

3/25/2026 Source: NEJM

Summary

Prime Editing for p47(phox)-Deficient Chronic Granulomatous Disease. Review Article Abstract Prime Editing for p47(phox)-Deficient Chronic Granulomatous Disease. Gori JL(1), Haddad E(2)(3), Frangoul H(4), Kohn DB(5), Morris EC(6), Martin BN(1), Deary BA(1), Nickerson M(1), Scholz RL(1), Fernandez I(2)(3), Leveille K(2)(3), De Ravin SS(7), Kang EM(7), Pierzynski M(7), Estwick T(7), Littel P(7), Kuhns DB(8), Long Priel DA(8), Teira P(2), Turvey S(9), Arnold J(5), Evans MD(4), McManus M(4), Ca

Content

# Prime Editing for p47(phox)-Deficient Chronic Granulomatous Disease. *Review Article* # Abstract Prime Editing for p47(phox)-Deficient Chronic Granulomatous Disease. Gori JL(1), Haddad E(2)(3), Frangoul H(4), Kohn DB(5), Morris EC(6), Martin BN(1), Deary BA(1), Nickerson M(1), Scholz RL(1), Fernandez I(2)(3), Leveille K(2)(3), De Ravin SS(7), Kang EM(7), Pierzynski M(7), Estwick T(7), Littel P(7), Kuhns DB(8), Long Priel DA(8), Teira P(2), Turvey S(9), Arnold J(5), Evans MD(4), McManus M(4), Carpenter B(10), Waterman DP(1), Anzalone AV(1), Petrusich A(1), Osuna CE(1), O'Malley TT(1), Stewart-Ornstein J(1), Heath JM(1), Nehilla BJ(1), Asmal M(1), Malech HL(7). --- DOI: 10.1056/NEJMoa2509807